High-efficiency base editing for #Stargardt disease in mice, non-human primates, and human #retina tissue https://www.biorxiv.org/content/10.1101/2023.04.17.535579v1 #ABCA4 #GeneTherapy, #CRISPR

👁️ #Stargardt disease is an eye condition that can cause blindness.

Although relatively rare, it affects about 1 in every 10 000 people.

Thanks to the #EUfunded Soraprazan project, a cure through a new regenerative therapy is now possible.

More 👉 https://europa.eu/!7W6Wfp

🐦🔗: https://nitter.eu/CORDIS_EU/status/1523979920598257664