Gene correction alone is not sufficient to treat spinal muscular atrophy (#SMA). But combining gene editing with gene supplementation shows promising results in mice.

First #preLight from Preethi Krishnaraj on work from a team #altos_labs. Check it out! 👀

preLight👉 https://prelights.biologists.com/highlights/therapeutic-strategy-for-spinal-muscular-atrophy-by-combining-gene-supplementation-and-genome-editing/