David R. Liu · @davidrliu
419 followers · 33 posts · Server mstdn.science

RT @jcornlab@twitter.com

causes devastating bone marrow failure. But HDR editing doesn't work in cells from these patients. In collaboration w/ @PauFerrol@twitter.com & funding @EJPRareDiseases@twitter.com we develop a approach for bone marrow cells from FA patients. nature.com/articles/s41467-022

🐦🔗: twitter.com/jcornlab/status/15

#FanconiAnemia #crispr #BaseEditing

Last updated 3 years ago