RT @jcornlab@twitter.com
#FanconiAnemia causes devastating bone marrow failure. But #CRISPR HDR editing doesn't work in cells from these patients. In collaboration w/ @PauFerrol@twitter.com & funding @EJPRareDiseases@twitter.com we develop a #BaseEditing approach for bone marrow cells from FA patients. https://www.nature.com/articles/s41467-022-34479-z
#FanconiAnemia #crispr #BaseEditing