Replay targets genetic brain disorders with new gene therapy company, Kaleibe, utilising big DNA HSV technology
#Biomedicine #GeneTherapy #GeneDelivery #MolecularTherapy #ViralVectors #HerpesviralVectors #HSV
#Neurogenetics #Parkinson #FriedreichAtaxia #Ataxia #NeurogeneticDiseases #GeneticDiseases #NeurologicalDiseases #NeurodegenerativeDiseases #BrainDiseases #Neurology #Neuroscience
https://replay.bio/news/replay-targets-genetic-brain-disorders
#neuroscience #neurology #BrainDiseases #NeurodegenerativeDiseases #NeurologicalDiseases #GeneticDiseases #NeurogeneticDiseases #ataxia #FriedreichAtaxia #parkinson #neurogenetics #hsv #HerpesviralVectors #ViralVectors #MolecularTherapy #GeneDelivery #genetherapy #biomedicine
RNA-Targeting Strategy to Repair Genetic Cause of ALS and Frontotemporal Dementia
A novel compound eliminates disease-causing segments of RNA associated with ALS and dementia, and restores the health of neurons in mouse models
#Neuroscience #Neurology #NeurodegenerativeDiseases #ALS #FTD #Dementia
#Genetics #GeneticDiseases #RareDiseases
#MolecularTherapy #ToxicRNA #RNAtargeting
#Biomedicine
#neuroscience #neurology #NeurodegenerativeDiseases #ALS #FTD #dementia #genetics #GeneticDiseases #RareDiseases #MolecularTherapy #ToxicRNA #RNAtargeting #biomedicine