🩸 @MonashUni say their new preventative treatment for #haemophilia could help patients stop bleeding

https://www.scimex.org/newsfeed/new-preventative-treatment-for-haemophilia-could-help-patients-stop-bleeding

RT @CathyAH1980@twitter.com

Looking forward to sharing our posters from the @SheffieldHosp@twitter.com #Haemophilia #nurses at #EAHAD2023 We're sharing a competency package for development of specialist nurses which has been adapted to encompass #bleedingdisorders, #ITP & #TTP & also our approach to staff #wellbeing https://twitter.com/EAHADnews/status/1613891142843764737

🐦🔗: https://twitter.com/CathyAH1980/status/1613965925845180419

"CSL’s Hemgenix costs $3.5mn per dose, which makes it the most expensive drug in the world. Skysona and Zynteglo, which are gene therapies targeting a rare childhood brain disease and an inherited blood disorder, developed by the Cambridge, Massachusetts-based biotech Bluebird Bio, are the second- and third-most expensive drugs on the market. They are priced at $3mn and $2.8mn per dose, respectively."

#GeneTherapy #DrugDiscovery #DrugDevelopment #haemophilia
#raredisease

https://www.ft.com/content/8173d816-1167-4773-bad5-f565fed3ffde